After applying for accelerated FDA approval of delpacibart zotadirsen in DMD, Avidity launched a confirmatory trial of the ...

In real-world use, the 4-week pegunigalsidase alfa regimen the EC recently approved for Fabry disease treatment appeared safe ...

Telomere-related gene variants contribute to idiopathic pulmonary fibrosis (IPF) susceptibility, according to a new study.

Finerenone was associated with reduced albuminuria and a slower eGFR decline in COQ8B-associated focal segmental ...

Concomitant IPF and lung cancer are associated with a substantially higher risk of mortality and respiratory health care burden, a study shows.

The international share of clinical trials conducted in the European Economic Area dropped from 22% to 12% in a decade.

A cross-sectional study of early-onset chronic obstructive pulmonary disease in Bangladesh identified AATD in 12.5% of patients.

The body composition of patients with IPF is associated with their risk of having diarrhea while being treated with nintedanib, a study shows.

Investigators are now recruiting people with Huntington disease (HD) for the phase 1 INSIGHTT trial of SRP-1005 at 2 sites in New Zealand.

Multidisciplinary support seems to be associated with better 1-year treatment continuation with nintedanib in patients with fibrosing ILDs.

In a small study of patients with HD who received PEG tubes, neither weight loss nor severe dysphagia predicted the timing of placement.

At this point, I simply would be happy to know: Whose job is it, anyway?